two independent medical team announced Sunday that the treatment of a rare genetic disorder of the blind – Lieber congenital amaurosis (LCA) of gene therapy has improved the vision of four patients, gene therapy techniques in order to give added hope.
LCA destroy the light receptors of the retina. In the early period of the disease began to affect the vision of patients at the age of 30 will be completely blind. There is no treatment. The two teams used a common cold virus, the disease will cause the normal version of the RPE65 gene directly into the eyes of patients.
researchers at the Florida meeting of ophthalmologists and the New England Journal of Medicine, published reports that, although the two sets of tests have detected only for security, but the patients reported that their visual acuity improved significantly.
Children's Hospital of Philadelphia and Howard